Despite diagnostic and therapeutic advances, mortality and the multi-systemic health impact of SMA continue to be experienced ...

Kuntz, MD, was a fellow about 45 years ago, there were few more devastating diagnoses than Duchenne muscular dystrophy (DMD).

Capricor Therapeutics’ plan to seek early approval for a stem cell therapy for patients with Duchenne muscular dystrophy is ...

Spinal muscular atrophy (SMA) is a disorder affecting the motor neurons—nerve cells that control voluntary muscle movement. These cells are located in the spinal cord. Because the muscles cannot ...

Zinc supplementation showed limited benefits in improving muscle health and hydration in boys with DMD. Nearly 30% of participants had low zinc levels initially, with slight improvement post ...

Patients with Duchenne muscular dystrophy (DMD) have long been without effective treatment options. Longstanding treatments such as corticosteroids and exon-skipping therapies can prolong the time it ...

Becker muscular dystrophy (BMD), an X-linked muscular dystrophy, is mostly caused by an in-frame deletion of DMD. BMD severity varies from asymptomatic to severe, associated with the genotype of DMD.

The Eu­ro­pean Med­i­cines Agency’s hu­man med­i­cines com­mit­tee again de­cid­ed not to rec­om­mend the re­new­al of the con­di­tion­al mar­ket­ing au­tho­riza­tion for ...

Opens in a new tab or window SAVANNAH, Ga. -- Delandistrogene moxeparvovec (Elevidys), a gene therapy approved to treat Duchenne muscular dystrophy, missed its primary endpoint but differences ...

George Stephanopoulos recently ignited chatter among his co-hosts by flaunting his muscular physique in a fitted T-shirt (Getty Images) NEW YORK CITY, NEW YORK: George Stephanopoulos has left his ...

We recently published a list of 10 Biggest Stocks with Negative Beta to Consider. In this article, we are going to take a look at where Wave Life Sciences (NASDAQ:WVE) stands against other biggest ...