The embryos were female, and Jenssen remembers the doctors assuring her that, because the Duchenne mutation is linked to the ...

Neu refix granted orphan disease designation (ODD) & rare pediatric disease designation (RPDD) by US FDA for treatment of ...

Important insights into the mechanisms behind Fuchs Endothelial Corneal Dystrophy (FECD), a common cause of age-related visual loss, have been revealed in a new study led by UCL researchers.

A Northern Ireland man, 31, with Duchenne Muscular Dystrophy – a progressive muscle wasting disease that affects skeletal ...

Six-year-old Cooper Wood was diagnosed with Duchenne muscular dystrophy earlier this year. When his parents applied for a one ...

TUCSON, Ariz. (KGUN) — Hudson Sanford is a seven-year-old boy that was diagnosed with Duchenne muscular dystrophy (DMD) when he was four years old. World Duchenne Awareness Day is celebrated on ...

The life expectancy for a person with muscular dystrophy (MD) depends on which type of MD they have. Some people live a full life with MD. Others, including those diagnosed with Duchenne muscular ...

A father from Lewes has walked the length of Hadrian’s Wall to raise more than £12,000 for Muscular Dystrophy UK. The charity announced that James Chubb, 41, completed the 84-mile journey in 31 hours.

On Tuesday, Dyne Therapeutics Inc. (NASDAQ:DYN) announced new clinical data from its ongoing Phase 1/2 DELIVER trial of DYNE-251 in patients with Duchenne muscular dystrophy (DMD) amenable to exon ...

Patients treated with 20 mg/kg of DYNE-251 Q4W had a mean absolute dystrophin expression of 3.71% of normal. Dyne is initiating registrational cohorts in the DELIVER trial and plans to provide an ...

After escaping a clinical hold several years back, Dyne Therapeutics has revealed new phase 1/2 data for its Duchenne muscular dystrophy (DMD) therapy DYNE-251. The readout notes several serious ...