WASHINGTON, Aug. 27, 2024 /PRNewswire/ -- Marking a significant milestone in improving the lives of children affected by Duchenne muscular dystrophy (Duchenne), Parent Project Muscular Dystrophy ...

Michelle C. Werner agonized over whether the gene therapy treatment Elevidys was right for her teenage son. But to him, the ...

Neu refix granted orphan disease designation (ODD) & rare pediatric disease designation (RPDD) by US FDA for treatment of ...

KUWAIT, Sept 11: Dr. Laila Bastaki, Head of the Genetic Diseases Center at the Ministry of Health, emphasized the importance of incorporating genetic testing for Duchenne muscular dystrophy (DMD) into ...

M01, has been awarded orphan drug and rare pediatric disease designations by the FDA for the treatment of Duchenne muscular dystrophy (DMD). The program leverages the company’s proprietary Alphastem ...

A possible gene therapy approval and a series of major trials readouts set the stage for a busy year of drug development in Duchenne muscular dystrophy.

We hypothesize that Duchenne muscular dystrophy and autism spectrum disorder/pervasive developmental disorder co-occur with a greater than random frequency. In this study, we set out to reject the ...

KUWAIT CITY, Sept 11: Assistant Undersecretary for Medical Support Services at the Ministry of Health, Dr. Abdullah Al-Fars, announced on Wednesday that Kuwait is the first country in the Middle East ...

World Duchenne Awareness Day is celebrated on September 7th every year Here’s Why Soda Cans Are Beveled on the Bottom See the ...

On Tuesday, Dyne Therapeutics Inc. (NASDAQ:DYN) announced new clinical data from its ongoing Phase 1/2 DELIVER trial of DYNE-251 in patients with Duchenne muscular dystrophy (DMD) amenable to exon ...

Hudson Sanford is a seven-year-old boy that was diagnosed with Duchenne muscular dystrophy (DMD) when he was four years old.