The FDA has given the green light to a clinical trial testing ATA-200, a gene therapy for limb-girdle muscular dystrophy ...

Over half of the people who contributed to the report (53%) said they feel financially insecure. 17% of those reported ...

These updates will also be presented at the American Society of Gene and Cell Therapy and Muscular Dystrophy Association 2024 Breakthroughs ... including Novartis' Zolgensma ® for children with spinal ...

On Tuesday, Dec. 3, the Muscular Dystrophy Family Foundation (MDFF) will play host to a free Trivia Night on Giving Tuesday, Dec. 3, the national day of charity giving. Trivia begins at 6:30 p.m. at ...

In-shoe sensors, AI and biomarkers will monitor muscular dystrophy and atrophy in children, adolescents and adults — with ...

Low bone mineral density (BMD) appears to be common among children with spinal muscular atrophy (SMA), especially if those ...

Pratteln, Switzerland, November 12, 2024 – Santhera Pharmaceuticals (SIX: SANN) announces the signing of an exclusive supply agreement with Ali Al Suwaidi Trading Est. (ASTE) for the treatment of ...

Jerry Lewis' childhood friend and former manager revealed the real reason he got the boot from the Muscular Dystrophy telethon after 45 years of hosting.

Duchenne Muscular Dystrophy (Duchenne) LYNX Phase 2 trial in boys with Duchenne: LYNX is a 2-part multi-center, dose-finding Phase 2 trial to evaluate the effect of sevasemten on safety, PK, and ...

Despite diagnostic and therapeutic advances, mortality and the multi-systemic health impact of SMA continue to be experienced ...