Gene therapy can effectively treat various diseases, but for some debilitating conditions like muscular dystrophies there is a big problem: size. The ...
Per management, both AOC 1086 and AOC 1072 have been designed to address the root causes of the genetic diseases ... programs ...
On Tuesday, Dec. 3, the Muscular Dystrophy Family Foundation (MDFF) will play host to a free Trivia Night on Giving Tuesday, Dec. 3, the national day of charity giving. Trivia begins at 6:30 p.m. at ...
In-shoe sensors, AI and biomarkers will monitor muscular dystrophy and atrophy in children, adolescents and adults — with ...
has partnered with MDA to support individuals and families affected by muscular dystrophy. The SAFD is proud to continue this ...
Pratteln, Switzerland, November 12, 2024 – Santhera Pharmaceuticals (SIX: SANN) announces the signing of an exclusive supply agreement with Ali Al Suwaidi Trading Est. (ASTE) for the treatment of ...
Investors consider Dyne Therapeutics' treatments for muscle diseases and strong cash position as a speculative Buy ...
People with Myotonic Dystrophy Type 1 (DM1), the most common adult-onset form of muscular dystrophy ... replicates many of the cardiac characteristics observed in the human disease. In this model we ...
The Muscular Dystrophy Association (MDA)’s Kickstart program has announced receipt of both U.S. orphan drug and rare pediatric disease designations in support of work for congenital myasthenic ...