Cystic fibrosis is a genetic disorder affecting the lungs and digestive system, causing thick, sticky mucus that can lead to infections. Gene therapy for CF aims to deliver a healthy CFTR gene to ...

In other words, people with CF are born with the disease, inheriting a copy of this gene from each parent, says Boyle. In case you missed: At 25 she found out she had the breast cancer gene.

Reference: XJ Wang et al. Mutation in the gene responsible for cystic fibrosis and predisposition to chronic rhinosinusitis in the general population. JAMA 284 (14):1814-1819 (2000).

New hope for cystic fibrosis patients without treatment options Gomperts has always been driven by a simple goal: finding better treatments for her patients. That pursuit has led her to spend over 20 ...

ReCode’s lead programs include RCT2100 for the treatment of the 10% of people with cystic fibrosis who have genetic mutations in the CFTR gene that do not respond to currently approved CFTR ...

BETHESDA, Md.--(BUSINESS WIRE)--Today, the Cystic Fibrosis Foundation announced that it will provide up to $15 million to Prime Medicine for preclinical research into gene editing for cystic ...

According to the Cystic Fibrosis Foundation, roughly 40,000 people in the United States have CF, which is considered a rare genetic disease. Annually, about 1,000 newborns are diagnosed with CF.

Could next-generation gene editing mean a cure for cystic fibrosis (CF)? There's been a lot of advancement on the disease in the last decade, but there are still those living with the disease who ...