According to the Mayo Clinic, muscular dystrophy is a group of diseases that cause loss of muscle mass and progressive ...
First patient dosed in Phase 1/Phase 2 LION-CS101 trial of AB-1003 in August 2023, with enrollment continuing Asklepios ...
Advancement of Fast Skeletal Muscle Troponin Activator Expands Pipeline of Muscle-Directed Drug Candidates SOUTH SAN ...
Researchers created a mouse model to study liver symptoms of myotonic dystrophy type 1, revealing how toxic RNA in the liver ...
Sarepta Therapeutics is advancing SRP-9003 gene therapy for LGMD, with phase 3 study results expected in early 2025. Learn ...
WHAT IT'S ABOUT The documentary "The Remarkable Life of Ibelin" tells the story of Mats Steen, a Norwegian man with Duchenne ...
News Medical on MSN12d
New insights into cardiac defects in Myotonic Dystrophy Type 1People with Myotonic Dystrophy Type 1 (DM1), the most common adult-onset form of muscular dystrophy, progressively lose ...
Brooke has been unstoppable raising awareness and funds for ALS research while introducing our entire family to a community of support with the Muscular Dystrophy Association.” Challenges Rare Disease ...
Nashville, Tennessee Friday, November 8, 2024, 13:00 Hrs [IST] ...
"For Duchenne muscular dystrophy, a devastating genetic disorder affecting young boys, securing both Orphan Drug and Rare Pediatric Disease Designations for Ifetroban from the FDA is a critical ...
Research Triangle Park, North Carolina Saturday, November 9, 2024, 13:00 Hrs [IST] ...
CK-089 increased muscle force and function in animal models of a neuromuscular disease characterized by muscle weakness, atrophy and fatigue, suggesting it may have therapeutic application to a ...
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